02 · Sizing & Access · Report type

Pricing Strategy Model reports, across indications

A 12-sheet pricing architecture built market by market: price ladder, international reference-price basket, value-based ICER, gross-to-net waterfall, launch sequencing, and revenue scenarios — not a single number, a re-runnable model.

Pricing Strategy Model reports across indications

Hereditary Angioedema
PSM
PSM Rare Disease PricingMedical Affairs

UK Hereditary Angioedema Pricing Strategy Model

Three NICE technology appraisals (TA606, TA738, TA1101) each carry a confidential Patient Access Scheme, so garadacimab's published £20,625 per-pen price is the only fully transparent figure in the class, and two MHRA-licensed agents still have no NICE-confirmed net price.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Spinal Muscular Atrophy
PSM
PSM Rare Disease Medical AffairsPricing

GCC Spinal Muscular Atrophy Pricing Strategy Model

NPHC's negotiated Zolgensma price runs $1.5-1.8M against $2.125M US list, but the real mechanism is a 24-month motor-milestone rebate, the same structure now anchoring risdiplam and nusinersen pricing across the Gulf.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Hereditary Angioedema
PSM
PSM Rare Disease PricingMedical Affairs

GCC Hereditary Angioedema Pricing Strategy Model

Lanadelumab tenders at SAR 300,000-400,000 a year, but NPHC has no routine formulary price at all; access runs through an individual-case bar only 30-40% of submissions clear, while private VHI approves at a materially lower documentation threshold.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
PNH
PSM
PSM Rare Disease Medical AffairsPricing

DE PNH Pricing Strategy Model

Iptacopan's substantial-benefit finding gave Germany real negotiating leverage over Novartis. Six months on, no negotiated net price has surfaced in the Lauer-Taxe — the pricing signal this model is built to catch before a launch-sequencing decision locks in the wrong assumption.

DE In-Market 24–32 pp PDF · Excel · PPT Read report →
PNH
PSM
PSM Rare Disease Medical AffairsPricing

UK PNH Pricing Strategy Model

NICE has cleared every modern PNH anti-complement therapy, from ravulizumab to crovalimab, through the standard £20,000-30,000 Technology Appraisal route rather than the more generous Highly Specialised Technologies threshold, each via a confidential patient access scheme.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Fabry Disease
PSM
PSM Rare Disease Medical AffairsPricing

US Fabry Disease Pricing Strategy Model

Fabrazyme's orphan-drug exclusion under the IRA shields it from Medicare price negotiation entirely, and no rebate or net-price figure is disclosed anywhere in the primary record for any Fabry therapy. The orphan exclusion, not a discount ladder, is what a Fabry pricing strategy has to be built around.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Obesity
PSM
PSM Metabolic Market AccessMedical AffairsPricing

US Obesity Pricing Strategy Model

Wegovy lists at roughly $1,349 a month, but CMS pays $274 for a 30-day semaglutide supply starting 2027, a 71% cut that applies to Ozempic, Rybelsus, and Wegovy alike. Tirzepatide sits outside the negotiation entirely, for now.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Type 2 Diabetes
PSM
PSM Metabolic Market AccessMedical AffairsPricing

US Type 2 Diabetes Pricing Strategy Model

Two IRA negotiation cycles have now cut across the T2D formulary: Januvia down 79% to $113, Jardiance down 66% to $197, Farxiga down 68% to $178 from January 2026, and semaglutide down 71% to $274 with Janumet and Tradjenta added for 2027.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Plaque Psoriasis
PSM
PSM Immunology Market AccessMedical AffairsPricing

US Plaque Psoriasis Pricing Strategy Model

Stelara's negotiated price falls to $4,695 from a $13,836 list, a 66% cut, effective January 2026, the same month ustekinumab biosimilars begin launching. Two separate pricing shocks land on one legacy biologic at once.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Gaucher Disease
PSM
PSM Rare Disease Medical AffairsPricing

US Gaucher Disease Pricing Strategy Model

Three IV enzyme replacement brands run ~$300,000/year with no generic rival, so preferred-ERT designation is the real pricing lever. Eliglustat's CYP2D6 gate and generic miglustat's trial-first rule complete the picture.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
PNH
PSM
PSM Rare Disease Medical AffairsPricing

US PNH Pricing Strategy Model

Iptacopan's ~$550,000 annual WAC sits roughly 71% above ICER's own $156,000-157,000 value-based benchmark, yet the orphan-drug exclusion keeps anti-C5 incumbents priced outside IRA's reach entirely, the two forces any new US PNH entrant must price against.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
IgA Nephropathy
PSM
PSM Rare Disease Medical AffairsPricing

US IgA Nephropathy Pricing Strategy Model

All five FDA-approved IgAN therapies clear the same prior-authorization gate, biopsy-confirmed diagnosis, UPCR 0.8-1.5 g/g, eGFR 30 or higher, RAS-blockade step-through, rather than a negotiated rebate table. No formal net-price data exists because access here runs on step-therapy criteria, not payer negotiation.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Cold Agglutinin Disease
PSM
PSM Rare Disease Medical AffairsPricing

US Cold Agglutinin Disease Pricing Strategy Model

Sutimlimab costs $259,000-$302,000 per patient per year, and a peer-reviewed analysis puts its ICER at $2.34M/QALY, standard of care favored in all 10,000 probabilistic-sensitivity iterations. The value gap, not a rival drug, sets the pricing discipline.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
IgA Nephropathy
PSM
PSM Rare Disease Medical AffairsPricing

GCC IgA Nephropathy Pricing Strategy Model

IgA nephropathy sits outside NPHC's genetic/orphan disease scope entirely, so there is no GCC formulary price to model. Budesonide clears case-by-case at SAR 80,000-120,000/year through hospital committees or private insurance; sparsentan is not yet tender-priced at all.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
PNH
PSM
PSM Rare Disease Medical AffairsPricing

FR PNH Pricing Strategy Model

HAS splits PNH into two tracks: ravulizumab holds SMR important and first-line, priced at €14,988.66 per 1100mg vial. Iptacopan cleared only ASMR III, restricted to second-line, its €29,590.96 box price negotiated against a manufacturer-declared population of 270 patients.

FR In-Market 24–32 pp PDF · Excel · PPT Read report →
IgA Nephropathy
PSM
PSM Rare Disease Medical AffairsPricing

UK IgA Nephropathy Pricing Strategy Model

NICE's accepted 20-35% PAS discount off budesonide's WAC sets the pricing floor sparsentan already clears too, against a £140-180M NHS budget ceiling once the ACEi/ARB gate narrows eligibility to 3,000-5,000 patients.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Dravet Syndrome
PSM
PSM Rare Disease Medical AffairsPricing

US Dravet Syndrome Pricing Strategy Model

Fintepla's weight-based list price runs roughly 3x Epidiolex, and payers work that gap through step-edit design layered on Part D pharmacy-benefit routing. No generic cannabidiol reaches the US market before the late 2030s.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Fabry Disease
PSM
PSM Rare Disease Medical AffairsPricing

UK Fabry Disease Pricing Strategy Model

Agalsidase beta runs an estimated £150-250K per patient per year against migalastat's £80-120K, a £70-130K annual switch saving NICE has already quantified but the NHS has not captured at scale, with pegunigalsidase's TA915 commercial arrangement now setting a third price point.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Dravet Syndrome
PSM
PSM Rare Disease Medical AffairsPricing

UK Dravet Syndrome Pricing Strategy Model

Both NHS-commissioned Dravet therapies cleared NICE's standard £20,000-30,000/QALY bar, not the ultra-rare HSS threshold, so a new entrant is held to the same cost-effectiveness bar the incumbents already cleared. Total NHS Dravet spend still runs a modest £9-16M.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Fabry Disease
PSM
PSM Rare Disease Medical AffairsPricing

GCC Fabry Disease Pricing Strategy Model

NPHC pays roughly SAR 1.2-2.4M per patient per year for enzyme replacement against SAR 400-600K for migalastat, a 72% differential that gives NPHC a direct financial incentive to switch eligible patients, capped almost entirely by a single-laboratory diagnostic bottleneck rather than by price.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Dravet Syndrome
PSM
PSM Rare Disease Medical AffairsPricing

GCC Dravet Syndrome Pricing Strategy Model

GCC Dravet pricing is an import-cost economics problem, not a rebate negotiation: cannabidiol's Schedule-1-equivalent narcotics classification adds USD 10-15K in compassionate-programme cost plus SAR 5-8K in import logistics, while stiripentol's non-narcotic status keeps it at SAR 30-50K through standard hospital import.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
ATTR Amyloidosis
PSM
PSM Rare Disease Medical AffairsPricing

US ATTR Amyloidosis Pricing Strategy Model

Tafamidis prices 12-17x above ICER's fair-value benchmark, yet the orphan-drug exclusion keeps it out of IRA negotiation. Acoramidis and pending generics, not Medicare, now set net price.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Sickle Cell Disease
PSM
PSM Rare Disease Medical AffairsPricing

US Sickle Cell Disease Pricing Strategy Model

Casgevy and Lyfgenia list at $2.2M and $3.1M, but CMS's Cell and Gene Therapy Access Model, Medicaid concentration, and a $1.5-1.9M ICER ceiling decide the realized net, not the sticker price.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
ATTR Amyloidosis
PSM
PSM Rare Disease Medical AffairsPricing

UK ATTR Amyloidosis Pricing Strategy Model

NICE's TA1121 cost-minimisation rule directs clinicians to whichever ATTR-CM stabiliser costs less. That rule, not the QALY threshold alone, now sets a new entrant's UK price ceiling.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
PNH
PSM
PSM Rare Disease Medical AffairsPricing

GCC PNH Pricing Strategy Model

GCC anti-C5 tender pricing already runs 40-60% of US WAC, anchored to whichever EU comparator prices lowest, then compounded with a further 10-20% negotiation discount. Iptacopan has to clear the same cascade, still 12-24 months from SFDA registration.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Sickle Cell Disease
PSM
PSM Rare Disease Medical AffairsPricing

UK Sickle Cell Disease Pricing Strategy Model

NICE rejected crizanlizumab at £733K-1.1M per QALY even with a PAS discount. Casgevy cleared only via a 10-year annuity at £165K/year, and any new non-gene agent must land near £15-25K/year to clear that same ceiling.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Pompe Disease
PSM
PSM Rare Disease Medical AffairsPricing

US Pompe Disease Pricing Strategy Model

Pompe ERT WAC runs near $400,000 a year, and the Pombiliti + Opfolda regimen splits across Medicare Part B and Part D. Zero ICER reviews exist today, with one expected in 2025 and a 12-month J-code lead time for any new entrant.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Myasthenia Gravis
PSM
PSM Rare Disease Medical AffairsPricing

US Myasthenia Gravis Pricing Strategy Model

ICER priced efgartigimod's value at $18,300-28,400 a year, under half its ~$418,400 assumed launch price, and that gap is hardening into a three-tier step-edit staircase across US commercial and Part B plans.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Breast Cancer HR+/HER2-
PSM
PSM Oncology Medical AffairsPricing

US Breast Cancer HR+/HER2- Pricing Strategy Model

Ibrance's Medicare-negotiated price takes effect a full year before Kisqali's and Verzenio's. Three clinically equivalent drugs, staggered IRA negotiation cycles, means Pfizer sets the reference point Novartis and Lilly then have to negotiate against.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
ATTR Amyloidosis
PSM
PSM Rare Disease Medical AffairsPricing

GCC ATTR Amyloidosis Pricing Strategy Model

GCC tafamidis pricing is not one number. Private-import pricing near SAR 820,000-850,000/year describes the pre-registration state; post-registration tender pricing near SAR 70,000-90,000 describes what follows.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Pompe Disease
PSM
PSM Rare Disease Medical AffairsPricing

UK Pompe Disease Pricing Strategy Model

NHS-commissioned alglucosidase alfa runs £200,000-350,000 per patient a year post-PAS. Avalglucosidase alfa's NICE TA821 recommendation carries a 20-30% WAC premium and a switch-population budget impact of just £2-4M a year.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Sickle Cell Disease
PSM
PSM Rare Disease Medical AffairsPricing

GCC Sickle Cell Disease Pricing Strategy Model

At 200,000-250,000 GCC patients, US or UK list pricing is commercially impossible. NPHC's own exceptional-access threshold caps a novel agent near SAR 8,000-20,000/year, a fraction of a $2.2M gene-therapy WAC.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Myasthenia Gravis
PSM
PSM Rare Disease Medical AffairsPricing

UK Myasthenia Gravis Pricing Strategy Model

No UK gMG biologic has ever cleared NICE at any price. Eculizumab's manufacturer withdrew before submitting an ICER, and efgartigimod's June 2025 rejection means a future entrant's price ladder starts from zero precedent, not a benchmark.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →
Spinal Muscular Atrophy
PSM
PSM Rare Disease Medical AffairsPricing

US Spinal Muscular Atrophy Pricing Strategy Model

Zolgensma's $2.125M sticker price obscures the real US SMA pricing lever: a 10-state Medicaid outcomes-based annuity paying $212,500 a year for ten years, set against chronic Spinraza and Evrysdi costs and a Part B/Part D routing split that changes patient cost by drug.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Pompe Disease
PSM
PSM Rare Disease Medical AffairsPricing

GCC Pompe Disease Pricing Strategy Model

NPHC's annual Pompe ERT budget runs SAR 100-160M across 80-120 patients, at SAR 800K-1.2M for alglucosidase versus SAR 1.2-1.8M for avalglucosidase. A new entrant should target SAR 2.0-2.5M a year, with switch approvals clearing at only 40-60%.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Myasthenia Gravis
PSM
PSM Rare Disease Medical AffairsPricing

GCC Myasthenia Gravis Pricing Strategy Model

GCC gMG has no single price. Efgartigimod costs SAR 300,000-600,000/yr through private VHI, a different figure through hospital pharmacy committees, and a third through NPHC exceptional access, with a unified formulary price still 12-18 months out.

GCC In-Market 24–32 pp PDF · Excel · PPT Read report →
Hereditary Angioedema
PSM
PSM Rare Disease PricingMedical Affairs

US Hereditary Angioedema Pricing Strategy Model

Lanadelumab lists near $450,000 a year against berotralstat's roughly $95,000, and ICER's 2021 fair-value benchmark for berotralstat lands almost exactly on that list price. The three 2025 entrants carry no ICER anchor of their own.

US In-Market 24–32 pp PDF · Excel · PPT Read report →
Spinal Muscular Atrophy
PSM
PSM Rare Disease Medical AffairsPricing

UK Spinal Muscular Atrophy Pricing Strategy Model

NICE rejected Zolgensma in 2021 on cost per QALY, then reversed in 2023 through its Long-Term Value Framework. That framework, not the PAS discount, is the real UK SMA pricing lever, and it sets an estimated £1.2-1.6M net cost against a £4.5-7.5M lifetime chronic-therapy alternative.

UK In-Market 24–32 pp PDF · Excel · PPT Read report →

Pricing Strategy Model — frequently asked

What formats are included?

An editable 12-sheet Excel pricing model and a PDF methodology brief, with a 45-minute analyst call included. No PowerPoint deck — this deliverable is built to be worked in directly, not presented from.

How is the pricing evidence verified?

Every reference price, rebate mechanism, and ICER input is cited to a primary regulatory or HTA source — no price point is carried from model memory.

Can I model a specific market basket or comparator set?

Yes. You set the market basket, comparator class, and WTP threshold; the model is built to your scope and delivered editable.