Rare Disease · United Kingdom · In-Market

UK ATTR Amyloidosis Pricing Strategy Model

NICE's TA1121 cost-minimisation rule directs clinicians to whichever ATTR-CM stabiliser costs less. That rule, not the QALY threshold alone, now sets a new entrant's UK price ceiling.

12-sheet modelPAS discount ladderIn-MarketUpdated Q3 2026
Market United States United Kingdom GCC (Gulf) Stage
The Landscape

NICE's TA1121 cost-minimisation rule, not the QALY threshold alone, now sets the UK ATTR-CM price ceiling: any new stabiliser must beat whichever of tafamidis and acoramidis is cheaper.

NICE recommended tafamidis (Vyndaqel/Vyndamax, Pfizer) for ATTR-CM under TA696 in 2021, since updated by TA984 in June 2024, on a confidential Patient Access Scheme estimated at a 40 to 50 percent discount off UK WAC. That discount brings the modelled cost per QALY within NICE's standard £20,000-30,000 threshold and sets an effective NHS price near £12,000-18,000 a year, built on the ATTR-ACT trial's mortality benefit and a modelled QALY gain of 0.7 to 1.2. Acoramidis (Beyonttra, Bayer) cleared its own NICE bar under TA1121 in January 2026, but without a head-to-head trial against tafamidis. NICE's committee went a step further than a standard cost-effectiveness sign-off and directed clinicians to use whichever of the two stabilisers is less expensive, once administration costs, dose, price per dose, and each drug's commercial arrangement are accounted for.

That cost-minimisation directive changes the pricing question for any third entrant. It is no longer enough to clear £20,000-30,000/QALY against a fixed comparator; a new stabiliser has to beat whichever of tafamidis and acoramidis is cheaper at the moment of appraisal, since NICE will simply direct prescribers to the lower-cost option again. Vutrisiran (Amvuttra, Alnylam) illustrates the ceiling from the silencer side: its list price alone runs near £383,000 a year, brought down by its own confidential Patient Access Scheme under TA868 for ATTR-PN and TA1115 for ATTR-CM. NHS England projects total ATTR-CM spend at £80-120 million a year once roughly 5,000 patients are on treatment, a budget-impact ceiling that any new commercial arrangement has to sit under.

£12K-18K
tafamidis's effective NHS price per year after its estimated 40-50% Patient Access Scheme discount, NICE TA984
£20K-30K
NICE's standard cost-per-QALY threshold that tafamidis's PAS-discounted price clears
£80-120M
projected annual NHS ATTR-CM spend at peak, roughly 5,000 patients on treatment
TA1121
NICE's cost-minimisation recommendation directing clinicians to the least expensive of tafamidis and acoramidis
PRICE LADDER MECHANICS

UK ATTR pricing — NICE's cost-minimisation rule already forces tafamidis and acoramidis into direct price competition

AgentNICE RouteList/WAC PriceEffective NHS Price
Vyndaqel/Vyndamax (tafamidis)TA984 (updating TA696)UK WAC (undisclosed)~£12,000-18,000/yr after ~40-50% PAS discount
Beyonttra (acoramidis)TA1121, Jan 2026Similar order to tafamidis WACDirected to match whichever stabiliser costs less, post-PAS
Amvuttra (vutrisiran)TA868 (ATTR-PN) / TA1115 (ATTR-CM)~£383,000/yr listConfidential PAS discount off list

Sources: NICE TA984 (tafamidis, updating TA696); NICE TA1121 (acoramidis, 14 January 2026); NICE TA868 and TA1115 (vutrisiran); NHS England ATTR-CM service commissioning documentation.

Commercial Questions

What this model answers

Every section answers a named commercial question your team is asking, scoped to your asset.

01
What Patient Access Scheme discount does a new ATTR-CM stabiliser need to clear NICE's £20,000-30,000/QALY threshold, given tafamidis's precedent?

Delivers

  • TA984 QALY modelling and PAS discount mechanics
  • the £12,000-18,000/year effective-price precedent
  • the corridor a new stabiliser's commercial arrangement has to land inside
02
How does NICE's TA1121 cost-minimisation directive change pricing strategy for a third stabiliser entering after tafamidis and acoramidis?

Delivers

  • TA1121's least-expensive-stabiliser mechanic explained
  • what it means for a new entrant that cannot rely on a fixed QALY comparator
  • commercial-arrangement structuring options
03
What NHS budget-impact ceiling should a new ATTR-CM entrant plan pricing against, given the £80-120 million peak-spend projection?

Delivers

  • NHS England's ATTR-CM spend projection at peak patient volume
  • vutrisiran's £383,000 list-to-PAS ladder as the silencer-side benchmark
  • budget-impact modelling for a new commercial arrangement

Custom model delivered in 72 hours.

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Contents

What's inside

Rare Disease · 24–32 pp · In-Market · Analyst report + Excel model + PowerPoint readout

1 The Binding Constraint 2 pp
  • Why TA1121's cost-minimisation rule, not the QALY threshold alone, decides a new stabiliser's UK price
  • Pressure-tested against tafamidis's and acoramidis's live PAS precedent before the rest of the model is built out
2 Price Ladder — PAS Discount to the £20K-30K/QALY Threshold 3 pp
  • How tafamidis's 40-50% PAS discount lands its effective price at £12,000-18,000/year
  • Where a new stabiliser's commercial arrangement needs to sit inside that corridor
3 TA1121's Cost-Minimisation Rule — Tafamidis vs Acoramidis 3 pp
  • How NICE's least-expensive-stabiliser directive works mechanically
  • What it means for pricing a third entrant with no head-to-head data
4 Analogue Benchmarks — Vutrisiran's £383K List-to-PAS Ladder 3 pp
  • Vutrisiran's list price and its TA868/TA1115 PAS discount as the silencer-side comparator
  • What the analogue supports for a new agent's own commercial-arrangement depth
5 Value-Based QALY Modelling & NICE Precedent 3 pp
  • How TA984's QALY gain of 0.7-1.2 was modelled
  • Where the evidence base could support a premium over the tafamidis/acoramidis floor
6 GTN Waterfall & PAS Discount Layers 3 pp
  • The WAC, PAS discount, and effective NHS price components decomposed line by line
  • The 40-50% discount depth already observed in TA984
7 Launch Sequencing & NHS Spend Scenarios 4 pp
  • Sequencing recommendation against the £80-120M peak-spend ceiling
  • Conservative, base, and aggressive NHS uptake scenarios
8 Client Alignment Questions 2 pp
  • The open pricing questions your team must close before the UK NICE submission is locked
  • Structured for an internal pricing committee session
Appendix and source ledger included · 45-minute analyst readout included with delivery
Formats

Included with every brief

PDF
PDF Brief
Pricing Strategy Brief — Complete Edition
PDF methodology brief accompanying the 12-sheet pricing model: PAS discount ladder, NICE's cost-minimisation rule, QALY modelling, and GTN waterfall for ATTR amyloidosis in the UK.
XLS
Excel Model
Pricing Strategy Model — Excel
12-sheet editable model: Price Ladder, QALY Modelling, Analogue Benchmarks, Value-Based Modelling, GTN Waterfall, Launch Sequencing, Revenue Scenarios, Sensitivity, NICE Landscape, QC, Sources.
Methodology

How AXLRx builds this model

Prepared by MoatRx analysts.

Every AXLRx pricing model is built from primary NICE technology appraisal documents and NHS England commissioning specifications, not secondary summaries. Findings are independently verified before inclusion.

UK ATTR pricing sources: NICE TA984 (tafamidis, updating TA696), NICE TA1121 (acoramidis, 14 January 2026), NICE TA868 and TA1115 (vutrisiran), and NHS England ATTR-CM service commissioning documentation.

  • Tafamidis's PAS discount estimate and £20,000-30,000/QALY clearance verified against the NICE TA984 decision document
  • TA1121's cost-minimisation directive for acoramidis verified against the NICE TA1121 final guidance, 14 January 2026
  • Vutrisiran's list price and PAS structure verified against NICE TA868 and TA1115 final guidance
FAQ

Frequently asked questions

Deliverables
What formats are included with every model?
Every commissioned Pricing Strategy Model includes an editable 12-sheet Excel model (Price Ladder, QALY Modelling, Analogue Benchmarks, Value-Based Modelling, GTN Waterfall, Launch Sequencing, Revenue Scenarios, Sensitivity, NICE Landscape, QC, Sources) and a PDF methodology brief. There is no PowerPoint deck: a pricing model is built to be worked in directly, not presented from. An optional 45-minute analyst readout call is included.
Sources
How is the pricing evidence verified?
AXLRx builds from primary sources only: NICE technology appraisal documents, NHS England commissioning specifications, and MHRA approval records. No secondary market-research summaries. Every PAS estimate, QALY figure, and NHS spend projection is independently verified before inclusion.
Customisation
Can I model a specific NICE pathway or comparator set?
Yes. The intake form captures your indication, target NICE pathway (STA, HST, MAA), comparator class, and QALY threshold assumption. A scoping call confirms scope before research starts. Commission through the intake form to begin.
Get Started

Commission this model

AXLRx delivers ATTR pricing strategy models built for market access and pricing teams navigating NICE's cost-minimisation rule and the NHS ATTR-CM budget ceiling. Custom model in 72 hours.

1
Submit your request

Specify your indication, target NICE pathway, and comparator scope.

2
Scoping call

AXLRx analyst confirms PAS and QALY-threshold assumptions before building.

3
Delivery

Research-verified pricing model in 72 hours with optional analyst readout.