Rare Disease · United Kingdom · In-Market

UK Myasthenia Gravis Pricing Strategy Model

No UK gMG biologic has ever cleared NICE at any price. Eculizumab's manufacturer withdrew before submitting an ICER, and efgartigimod's June 2025 rejection means a future entrant's price ladder starts from zero precedent, not a benchmark.

8-sheet modelNICE threshold modellingIn-MarketUpdated Q3 2026
Market United States United Kingdom GCC (Gulf) Stage
The Landscape

No UK gMG biologic has ever cleared NICE at any price. Two consecutive appraisals ended without a positive recommendation, so a future entrant's price ladder has to be modelled from the IVIg cost-offset up, not from a cleared precedent down.

Eculizumab's NICE appraisal for refractory myasthenia gravis was terminated in June 2020 after the manufacturer withdrew without submitting a cost-effectiveness dossier; no cost-per-QALY figure was ever modelled or published for the drug in this indication. Efgartigimod's appraisal concluded differently but with the same result: NICE's final guidance, published 4 June 2025, does not recommend the drug for NHS use, citing gaps and uncertainties in the cost-effectiveness evidence rather than a specific quantified ICER breach, despite a 68% MG-ADL responder rate in the ADAPT trial. Rozanolixizumab's NICE appraisal has not yet been initiated, leaving it as the FcRn class's one still-open bid. A new entrant's pricing strategy therefore starts from a genuinely blank precedent rather than a benchmark to beat.

The strongest unused lever for a future submission is the NHS IVIg cost offset: an estimated £40-60 million a year is spent on immunoglobulin for gMG across roughly 4,000 patients, with supply constrained under the NHS-wide IVIg prioritisation programme. Modelling that offset against a target WAC of £80-120,000 a year, with a 45-55% patient access scheme discount, implies an effective NHS price of £40,000-78,000 a year, crediting an IVIg cost-offset of £5,000-10,000 per patient per year plus subcutaneous administration savings of £3,000-5,000 per patient per year versus IV. Subcutaneous formulation is not optional for a competitive submission on these numbers.

0
NICE-recommended novel biologics for UK gMG today, despite two separate appraisals reaching a conclusion
£80-120K
modelled target WAC/yr for a future gMG entrant to have a realistic chance of clearing NICE's threshold
45-55%
patient access scheme discount modelled off WAC to reach an NHS-acceptable effective price
£40-78K
resulting effective NHS price/year once IVIg cost-offset (£5,000-10,000/patient/yr) and SC-administration savings are credited
PRICE LADDER MECHANICS

UK gMG pricing — from zero precedent to a modelled NHS-acceptable price

Agent / ScenarioNICE StatusReference MechanismEstimated NHS-Acceptable Price
EculizumabAppraisal terminated 2020; no ICER ever modelledManufacturer withdrew before evidence submissionNo NICE-cleared price exists; Individual Funding Request access only
EfgartigimodNot recommended, June 2025Cost-effectiveness evidence judged too uncertain at the submitted priceWould need a resubmission at a materially lower net price or a managed-access proposal
Future entrant (modelled)Not yet appraisedTarget WAC £80-120K/yr, 45-55% PASEffective NHS price £40-78K/yr, crediting IVIg and SC-administration offsets

Sources: NICE eculizumab MG termination decision document; NICE efgartigimod final guidance (not recommended, June 2025); ADAPT trial MG-ADL data; NHS England IVIg demand and prioritisation programme documentation.

Commercial Questions

What this model answers

Every section answers a named commercial question your team is asking, scoped to your asset.

01
Why did eculizumab's appraisal end without a price review while efgartigimod's ended with an outright rejection, and what does each failure mode mean for pricing strategy?

Delivers

  • The two termination mechanisms compared
  • why efgartigimod's evidence-uncertainty rejection is the more informative precedent for a future submission
  • rozanolixizumab's still-open bid as the class's remaining test case
02
What WAC and PAS combination clears NICE's cost-effectiveness threshold once the IVIg cost-offset is credited into the model?

Delivers

  • Target WAC £80-120K/yr and PAS 45-55% modelling
  • the £40-78K effective-price range this implies
  • SC-versus-IV administration-cost offset mechanics
03
How large is the NHS IVIg cost-offset argument, and how should it be built into a resubmission or new entrant's NICE dossier?

Delivers

  • £40-60M/yr NHS IVIg spend across ~4,000 patients
  • the IVIg prioritisation programme's supply-constraint context
  • the offset argument structure a submission should lead with

Custom model delivered in 72 hours.

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Contents

What's inside

Rare Disease · 24–32 pp · In-Market · Analyst report + Excel model + PowerPoint readout

1 The Binding Constraint 2 pp
  • Why no UK gMG biologic has ever cleared NICE at any price, and what that means for a first-mover pricing strategy
  • Pressure-tested against both prior appraisal outcomes before the rest of the model is built out
2 Price Ladder — NICE Cost-Effectiveness Threshold Mechanism 3 pp
  • How a WAC and PAS combination must translate into an NHS-acceptable ICER
  • Where the evidence-uncertainty rejection differs from a cost-per-QALY failure
3 Two Failure Modes — Withdrawal Versus Rejection 3 pp
  • Eculizumab's manufacturer withdrawal before any evidence was submitted
  • Efgartigimod's evidence-uncertainty rejection despite a 68% MG-ADL responder rate
4 Analogue Benchmarks — Rozanolixizumab's Open NICE Bid 3 pp
  • The FcRn class's one still-untested appraisal
  • What a positive rozanolixizumab outcome would set as the class's first price precedent
5 IVIg Cost-Offset & GTN Waterfall 3 pp
  • The £40-60M/yr NHS IVIg spend as the strongest unused pricing lever
  • GTN waterfall components decomposed against the IVIg-offset and SC-administration savings
6 Target WAC/PAS Modelling 3 pp
  • £80-120K/yr target WAC and 45-55% PAS scenario grid
  • The £40-78K/yr effective-price range this implies
7 Launch Sequencing & Revenue Scenarios 4 pp
  • Resubmission-versus-new-entrant sequencing options
  • Conservative, base, and aggressive revenue scenarios tied to a first positive NICE outcome
8 Client Alignment Questions 2 pp
  • The open pricing questions your team must close before a NICE submission is locked
  • Structured for an internal pricing committee session
Appendix and source ledger included · 45-minute analyst readout included with delivery
Formats

Included with every brief

PDF
PDF Brief
Pricing Strategy Brief — Complete Edition
PDF methodology brief accompanying the 8-sheet pricing model: NICE threshold mechanism, the two prior appraisal failure modes, IVIg cost-offset, and target WAC/PAS modelling for UK myasthenia gravis.
XLS
Excel Model
Pricing Strategy Model — Excel
8-sheet editable model: Price Ladder, NICE Threshold Mechanism, Analogue Benchmarks, IVIg-Offset GTN Waterfall, WAC/PAS Scenario Grid, Launch Sequencing, Revenue Scenarios, Sources.
Methodology

How AXLRx builds this model

Prepared by MoatRx analysts.

Every AXLRx pricing model is built from primary regulatory sources, published NICE appraisal and guidance documents, and NHS commissioning data, not secondary summaries. Findings are independently verified before inclusion.

UK myasthenia gravis pricing sources: NICE's eculizumab termination decision document, NICE's efgartigimod final guidance, ADAPT trial evidence, and NHS England IVIg demand-management programme data.

  • Eculizumab's appraisal-termination rationale and efgartigimod's rejection rationale verified against the published NICE decision documents
  • NHS IVIg spend and patient-count figures verified against NHS England IVIg demand-management programme documentation
  • Target WAC and PAS modelling cross-checked against the effective-price ranges implied by comparable NICE rare-disease appraisals
FAQ

Frequently asked questions

Deliverables
What formats are included with every model?
Every commissioned Pricing Strategy Model includes an editable 8-sheet Excel model (Price Ladder, NICE Threshold Mechanism, Analogue Benchmarks, IVIg-Offset GTN Waterfall, WAC/PAS Scenario Grid, Launch Sequencing, Revenue Scenarios, Sources) and a PDF methodology brief, no PowerPoint deck, since a pricing model is built to be worked in directly rather than presented from. An optional 45-minute analyst readout call is included.
Sources
How is the pricing evidence verified?
AXLRx builds from primary sources only: published NICE appraisal and guidance documents, NHS commissioning and demand-management data, and peer-reviewed trial publications. No secondary summaries or market research reports.
Customisation
Can I model a resubmission scenario for a specific asset?
Yes. The intake form captures your asset, prior appraisal history if any, and target WAC/PAS range. A scoping call confirms scope before research starts. Commission via the intake form to start.
Get Started

Commission this model

AXLRx delivers myasthenia gravis pricing strategy models built for market access and pricing teams navigating the UK's zero-precedent NICE landscape. Custom model in 72 hours.

1
Submit your request

Specify your asset, prior NICE history if any, and target WAC/PAS range.

2
Scoping call

AXLRx analyst confirms pricing mechanism assumptions and IVIg-offset scope before building.

3
Delivery

Research-verified pricing model in 72 hours with optional analyst readout.