Rare Disease · United Kingdom · In-Market

UK PNH KOL Mapping

Five NHS Highly Specialised Services centres, anchored by the Leeds National PNH Service, concentrate fewer than 25 consultants managing over 90% of the UK's PNH caseload. That kind of institutional concentration is exactly the signal this workbook sizes before any individual name enters it.

6-sheet workbookK1-K6 gatesIn-MarketUpdated Q3 2026
Market GCC (Gulf) United Kingdom France Stage
The Landscape

Fewer than 25 UK consultants across five NHS centres manage more than 90% of the country's PNH patients, evidence of how concentrated this KOL network really is.

UK PNH expertise sits inside a small, NHS-defined network rather than a broad specialist field. NHS England commissions PNH complement-inhibitor therapy through 15 Highly Specialised Services-designated centres, with the bulk of the country's caseload concentrated at five anchor institutions: Leeds (home to the Leeds National PNH Service, the UK's single national registry and coordinating centre), King's College Hospital, Oxford, Addenbrooke's, and Glasgow. Fewer than 25 consultants across this network manage more than 90% of the roughly 600 patients on complement inhibitor therapy that the Leeds registry tracks. That level of concentration does not happen by accident; it reflects a deliberate NHS commissioning structure built around named designated centres. Our KOL Universe gate (K1) starts by mapping exactly this institutional structure before any single physician is scored.

That structure changes how AXLRx tiers influence in the UK. A consultant practicing at the Leeds coordinating centre, which runs the national registry underpinning NICE's own technology appraisal evidence base, carries different scientific weight than one at a non-designated district hospital, and our Tier Classification gate (K2) scores that distinction directly, alongside registry-authorship history and multidisciplinary aplastic-anaemia co-management experience (roughly 30% of UK PNH patients present with concurrent aplastic anaemia requiring dual management across the 15 JACIE-accredited NHS BMT centres). No named individual enters the workbook without a verification tag. Every KOL identity is checked against live publication records and institutional affiliations, then marked Verified, Industry benchmark, or Requires client validation.

5
anchor NHS centres, Leeds, King's College Hospital, Oxford, Addenbrooke's, and Glasgow, concentrating the bulk of UK PNH prescribing
<25
UK consultants who manage more than 90% of the country's PNH patients (NHS England HSS specification 2022)
~600
UK patients on complement inhibitor therapy tracked by the Leeds National PNH Registry, the coordinating anchor of the KOL network
15
JACIE-accredited NHS BMT centres providing dual management for the ~30% of UK PNH patients with concurrent aplastic anaemia
NHS CENTRE STRUCTURE

The UK PNH NHS network, five anchor centres across England and Scotland

InstitutionCityRole in Network
Leeds National PNH ServiceLeedsCoordinating national referral centre; single national registry
King's College HospitalLondonNHS Highly Specialised Services-designated centre
Oxford University HospitalsOxfordNHS Highly Specialised Services-designated centre
Addenbrooke's HospitalCambridgeNHS Highly Specialised Services-designated centre
Queen Elizabeth University HospitalGlasgowNHS Highly Specialised Services-designated centre (Scotland)

Sources: NHS England Highly Specialised Services specification for PNH (2022); Leeds National PNH Registry annual data as reported by the Leeds National PNH Service; MHRA and NICE TA698/TA1000 commissioning documentation.

Commercial Questions

What this workbook answers

Every section answers a named commercial question your team is asking, scoped to your asset.

01
Which NHS institutions actually concentrate UK PNH prescribing, and how few consultants sit behind that network?

Delivers

  • The five-centre NHS HSS structure (Leeds, King's, Oxford, Addenbrooke's, Glasgow)
  • consultant concentration as a KOL-tiering signal
  • K1 KOL Universe Sizing methodology
02
How does AXLRx tier scientific influence across a registry-coordinated NHS network without relying on publication count alone?

Delivers

  • K2 Tier Classification methodology
  • Leeds registry authorship and aplastic-anaemia co-management weighting
  • K3 Scientific Influence scoring inputs
03
What verification standard does every named KOL have to clear before shipping in the workbook?

Delivers

  • The three-tag verification protocol (Verified/Industry benchmark/Requires client validation)
  • live publication and institutional-affiliation cross-checks
  • why no placeholder name ships unflagged

Custom workbook delivered in 72 hours.

Commission This Workbook
Contents

What's inside

Rare Disease · 24–32 pp · In-Market · Analyst report + Excel model + PowerPoint readout

1 The Binding Constraint 2 pp
  • Why institutional concentration, not scattergun individual outreach, is the single variable this workbook sizes first
  • Pressure-tested against the five-centre NHS network case before the rest of the workbook is built out
2 KOL Universe (K1) 4 pp
  • Every UK PNH KOL sized and sourced from publication and institutional-affiliation data
  • The five-centre NHS HSS network, anchored by Leeds, as the sizing anchor
  • Universe boundaries: who counts as a KOL versus a high-volume prescriber
3 Tier Classification (K2) 3 pp
  • Scientific-influence scoring across registry authorship and aplastic-anaemia co-management capability
  • What separates a Tier 1 KOL from a high-volume district prescriber
4 Scientific Influence (K3) 3 pp
  • Influence inputs: Leeds registry authorship, NICE evidence-submission history, institutional role
  • Cross-checked against independent publication and citation data
5 Engagement Readiness (K4) 3 pp
  • Readiness scoring and channel recommendations per KOL
  • Sequencing implications for MSL deployment
6 MSL Territory Coverage (K5) 3 pp
  • Territory-to-KOL coverage map across England (Leeds, London, Oxford, Cambridge) and Scotland (Glasgow)
  • Where current MSL deployment has gaps, including Wales and Northern Ireland
7 Cross-Border Network (K6) 3 pp
  • Multi-market reach for KOLs active beyond the UK, across EU5 and wider international registries
  • Implications for coordinated versus purely local engagement
8 Client Alignment Questions 2 pp
  • The open KOL-engagement questions your medical affairs team must close
  • Structured for an internal alignment session before MSL deployment
Appendix and source ledger included · 45-minute analyst readout included with delivery
Formats

Included with every brief

PDF
PDF Brief
KOL Mapping Brief — Summary Edition
PDF summary brief: tier strip, KOL universe table, and geographic breakdown for UK PNH.
XLS
Excel Model
KOL Mapping Workbook — Excel
6-sheet editable workbook: KOL Universe, Tier Scoring, Engagement Calendar, MSL Territory, Cross-Border Network, Evidence Register.
Methodology

How AXLRx builds this workbook

Prepared by MoatRx analysts.

Every AXLRx KOL workbook is built from live publication records and institutional-affiliation data, not secondary summaries. No KOL name ships without a verification tag.

UK PNH KOL sources: NHS England Highly Specialised Services specification for PNH (2022); Leeds National PNH Registry annual data as reported by the Leeds National PNH Service; and the institutional affiliations named in NICE's TA698 and TA1000 appraisal documentation.

  • NHS HSS centre list and consultant-concentration figures verified against NHS England Highly Specialised Services specification for PNH (2022)
  • Leeds National PNH Registry patient counts and aplastic-anaemia overlap figures verified against Leeds National PNH Service reporting
  • Every KOL entry in the underlying workbook carries a three-tag verification status before delivery: Verified, Industry benchmark, or Requires client validation
FAQ

Frequently asked questions

Deliverables
What formats are included with every workbook?
Every commissioned KOL Mapping workbook includes an editable 6-sheet Excel workbook (KOL Universe, Tier Scoring, Engagement Calendar, MSL Territory, Cross-Border Network, Evidence Register) and a PDF summary brief. No PowerPoint deck: this deliverable is built to be worked in directly. An optional 45-minute analyst readout call is included.
Sources
How are KOL identities and rankings verified?
Every KOL entry is built from live publication and institutional-affiliation data, then tagged Verified, Industry benchmark, or Requires client validation. No name ships unverified.
Customisation
Can I scope this to a specific institution set or region?
Yes. The intake form captures your indication, geography, and institution scope. A scoping call confirms scope before research starts. Commission via the intake form to start.
Get Started

Commission this workbook

AXLRx delivers KOL mapping workbooks built for medical affairs and commercial teams engaging UK PNH specialists. Custom workbook in 72 hours.

1
Submit your request

Specify your indication, geography, and institution scope.

2
Scoping call

AXLRx analyst confirms institution scope and verification standard before building.

3
Delivery

Research-verified KOL workbook in 72 hours with optional analyst readout.