Rare Disease · United Kingdom · In-Market

UK Myasthenia Gravis Patient Flow Model

12,000-15,000 UK gMG patients on the broader estimate, of whom ~4,000 have moderate-severe disease and 2,000-3,000 are refractory, with no NICE-recommended novel agent for any of them.

8-sheet modelLive patient funnelIn-MarketUpdated Q3 2026
Market United States United Kingdom GCC (Gulf) Stage
The Landscape

UK gMG prevalence spans a wide range depending on how broadly the population is defined, and reconciling that range, not picking one number, is the first step of a defensible funnel.

Two AXLRx research angles produce different UK gMG prevalence figures, and the difference is a scope difference, not a contradiction. The narrower estimate, 7,000-10,000 patients, comes from disease-landscape research anchored to the NHS neuromuscular network and the Myasthenia Gravis Association UK's registered membership, a base that captures patients in active specialist follow-up. The broader estimate, 12,000-15,000 patients, comes from launch-readiness population modelling and includes mild and well-controlled cases that are managed in primary or general neurology care and are not routinely captured in the specialist-network count. This model takes the broader 12,000-15,000 figure as total UK prevalence and treats the narrower estimate as the specialist-engaged subset within it.

Within that total, approximately 4,000 patients have moderate-to-severe disease and currently have no NICE-recommended novel agent, a segment confirmed independently across both research angles. A further 2,000-3,000 patients are specifically refractory to immunosuppressant therapy, the population launch-readiness modelling treats as the addressable pool for a new biologic. Roughly 30-40% of UK gMG patients, per Myasthenia Gravis Association UK survey data, report inadequate disease control on current standard therapy, a figure that applies most directly to the moderate-severe tier rather than the full 12,000-15,000 base.

12,000-15,000
total UK gMG prevalence on the broader population estimate, reconciled against a narrower 7,000-10,000 specialist-network figure
~4,000
UK moderate-to-severe gMG patients with no NICE-recommended novel agent
2,000-3,000
UK refractory gMG patients, the addressable pool for a new biologic entrant
THE FUNNEL

UK gMG funnel - reconciling total prevalence to the refractory, novel-agent-eligible pool

Funnel StagePopulationSource
Estimated total UK gMG prevalence (broad base)12,000-15,000AXLRx Launch Readiness research base
Specialist-network-confirmed subset (narrower base)7,000-10,000Myasthenia Gravis Association UK annual report 2023
Moderate-to-severe disease~4,000Myasthenia Gravis Association UK / AXLRx Launch Readiness research base
Refractory to immunosuppressant therapy2,000-3,000AXLRx Launch Readiness research base

Sources: Myasthenia Gravis Association UK annual report 2023; AXLRx Myasthenia Gravis UK Launch Readiness research base (MAGS UK survey methodology, NHSBT IVIg demand data 2023).

Commercial Questions

What this model answers

Every section answers a named commercial question your team is asking, scoped to your asset.

01
Why do UK gMG prevalence estimates range from 7,000-10,000 to 12,000-15,000, and which should a forecast use?

Delivers

  • The scope difference between the specialist-network-confirmed base and the broader population estimate
  • how each maps to a forecasting funnel
  • why 12,000-15,000 is used as total prevalence here
02
How large is the moderate-severe and refractory UK gMG population, and what share reports inadequate disease control?

Delivers

  • Moderate-severe sizing (~4,000)
  • refractory sizing (2,000-3,000)
  • the 30-40% inadequate-control rate from Myasthenia Gravis Association UK survey data
03
What does the live, re-runnable funnel model contain, and how is every conversion step sourced?

Delivers

  • 8-sheet structure (Strategic Context, Inputs, Model, Projections, Sensitivity, References, Market Context, QC)
  • primary-source citation per conversion step across both research angles

Custom model delivered in 72 hours.

Commission This Model
Contents

What's inside

Rare Disease · 24–32 pp · In-Market · Analyst report + Excel model + PowerPoint readout

1 The Binding Constraint 2 pp
  • Reconciling the 7,000-10,000 specialist-network estimate against the 12,000-15,000 population base
  • Pressure-tested before the rest of the model is built out
2 Disease Burden (E1) - Total Prevalence 3 pp
  • 12,000-15,000 estimated total UK prevalence
  • The narrower 7,000-10,000 specialist-network subset
3 Diagnosis & Capture (E2) - NHS Neuromuscular Network 3 pp
  • The 30-centre NHS neuromuscular network
  • Serological confirmation pathway
4 Severity Segmentation (E3) - Moderate-Severe Tier 4 pp
  • ~4,000 patients with moderate-to-severe disease
  • 30-40% reporting inadequate disease control (MGA UK survey)
5 Market Access (E4) - Refractory Population 3 pp
  • 2,000-3,000 refractory patients
  • No NICE-recommended novel agent for any tier
6 Sensitivity Analysis 3 pp
  • Which population-scope assumption moves the addressable pool most
  • Scenario ranges across the two prevalence estimates
7 Year 1·3·5 Projections 4 pp
  • Patient volume by horizon under conservative, base, and aggressive scenarios
  • Revenue translation inputs
8 Client Alignment Questions 2 pp
  • The open questions your forecasting team must close before the model is finalised
  • Structured for an internal forecast-review session
Appendix and source ledger included · 45-minute analyst readout included with delivery
Formats

Included with every brief

PDF
PDF Brief
Patient Flow Brief - Complete Edition
PDF methodology brief accompanying the 8-sheet funnel model: prevalence reconciliation, moderate-severe segmentation, and refractory-population sizing for UK gMG.
XLS
Excel Model
Patient Flow Model - Excel
8-sheet editable funnel model: Strategic Context, Inputs, Model, Projections, Sensitivity, References, Market Context, QC.
PPT
PowerPoint
Executive Readout - PowerPoint
12-15 slide readout deck for forecasting and launch team presentations, formatted to AXLRx design standards.
Methodology

How AXLRx builds this model

Prepared by MoatRx analysts.

Every AXLRx patient flow model is built on a five-layer funnel: population, disease burden (E1), diagnosis and specialist capture (E2), treatment and biomarker eligibility (E3), market access (E4), then Year 1-3-5 projections across three scenarios. Where two AXLRx research angles produce different population figures, this model states the scope difference explicitly rather than silently picking one number.

UK gMG sources: Myasthenia Gravis Association UK annual report and survey data, and the population and severity-segmentation research built for the AXLRx UK Launch Readiness assessment, which draws on NHSBT IVIg demand data and NHS neuromuscular network mapping.

  • Total UK prevalence range (12,000-15,000) and the narrower specialist-network estimate (7,000-10,000) verified against the AXLRx Launch Readiness and Disease Landscape research bases respectively
  • Moderate-to-severe population (~4,000) and 30-40% inadequate-control rate verified against Myasthenia Gravis Association UK survey data
  • Refractory population (2,000-3,000) verified against the AXLRx Launch Readiness research base
FAQ

Frequently asked questions

Deliverables
What formats are included with every model?
Every commissioned Patient Flow Model includes an editable 8-sheet Excel funnel model, a PDF methodology brief, and an optional executive readout deck for forecasting and launch team presentations. A 45-minute analyst readout call is included.
Sources
How does AXLRx handle two research angles that produce different prevalence figures?
AXLRx states the scope difference explicitly rather than silently choosing one number. The broader population estimate is used as total prevalence, and the narrower specialist-network estimate is presented as a defined subset within it, with both figures sourced.
Customisation
Can I tailor the cohort definition or comparator set?
Yes. The intake form captures your indication, target market, cohort definition, and comparators. A scoping call confirms scope before research starts.
Get Started

Commission this model

AXLRx delivers rare-disease patient flow models built for forecasting and launch teams sizing the UK gMG opportunity. Custom model in 72 hours.

1
Submit your request

Specify your indication, market, and cohort definition.

2
Scoping call

AXLRx analyst confirms funnel scope and comparator set before building.

3
Delivery

Research-verified patient flow model in 72 hours with optional analyst readout.