Rare Disease · United Kingdom · In-Market

UK ATTR Amyloidosis Patient Flow Model

True UK ATTRwt-CM prevalence runs 20,000-40,000, and 15,000-36,000 of those patients remain undiagnosed. Only 3,000-4,000 are on NHS-commissioned tafamidis today, adding 1,500-2,000 a year.

8-sheet model2 sub-populations sizedIn-MarketUpdated Q3 2026
Market United States United Kingdom GCC (Gulf) Stage
The Landscape

True UK ATTRwt-CM prevalence runs 20,000-40,000. Even after four years of NHS Tc-PYP commissioning, 15,000-36,000 of those patients remain undiagnosed.

The UK ATTR-CM funnel starts with a diagnostic pathway that did not exist before 2021. NHS England established the Tc-PYP scintigraphy commissioning route that year, and roughly 30 NHS scintigraphy centres are now active, producing 2,000-5,000 new ATTR-CM diagnoses a year, up from fewer than 500 a year before Tc-PYP availability. That growth looks fast against its own baseline, but it is small against true prevalence: true UK ATTRwt-CM prevalence is estimated at 20,000-40,000 patients, which leaves 15,000-36,000 undiagnosed even today. NICE's TA696 (2021), updated by TA984 (2024), commissioned tafamidis across NHS England Highly Specialised Cardiology services, and 3,000-4,000 patients are on treatment now, adding 1,500-2,000 a year as the diagnosed pool grows.

A smaller hereditary population sits beside ATTRwt-CM. ATTRv affects an estimated 1,000-2,000 UK patients, of whom roughly 800 are tracked in the UK National ATTRv Registry, led by UCL and Queen Elizabeth Hospital Birmingham. Val30Met is the most common variant, concentrated in Portuguese- and Brazilian-origin families in the UK, alongside Irish Thr60Ala families, and NHS GMS offers free TTR gene panel testing for probands with clinical features. The rate-limiting step across both populations is the same: growing the Tc-PYP referral pathway from NHS echo labs, which today reaches only around 50 of the relevant NHS cardiac centres, ahead of any question about drug access or NICE cost-effectiveness.

20,000-40,000
True UK ATTRwt-CM prevalence estimate, of which 15,000-36,000 remain undiagnosed
3,000-4,000
UK patients on NHS-commissioned tafamidis today (NICE TA984), growing 1,500-2,000/year
2,000-5,000/yr
New UK ATTR-CM diagnoses per year since the 2021 NHS Tc-PYP scintigraphy pathway, up from under 500/year before
~800
UK ATTRv (hereditary) patients tracked in the UK National ATTRv Registry, against an estimated 1,000-2,000 total
THE FUNNEL

UK ATTR amyloidosis funnel — from true prevalence to the NHS-treated pool

Funnel StagePopulationSource
True UK ATTRwt-CM prevalence20,000-40,000AXLRx ATTR launch-readiness research base (UK)
Undiagnosed ATTRwt-CM15,000-36,000AXLRx ATTR launch-readiness research base (UK)
On NHS-commissioned tafamidis today3,000-4,000, +1,500-2,000/yrAXLRx ATTR launch-readiness research base (UK); NICE TA984
New ATTR-CM diagnoses per year since 2021 Tc-PYP pathway2,000-5,000/yrAXLRx ATTR disease-landscape research base (UK)
ATTRv (hereditary) patients vs registry-tracked1,000-2,000 vs ~800AXLRx ATTR disease-landscape research base (UK); UK National ATTRv Registry

Sources: AXLRx ATTR amyloidosis disease-landscape, competitive-intelligence, payer-HTA, and launch-readiness research base (UK), synthesized for this funnel.

Commercial Questions

What this model answers

Every section answers a named commercial question your team is asking, scoped to your asset.

01
How large is the true UK ATTRwt-CM undiagnosed pool, and how fast is NHS Tc-PYP commissioning closing it?

Delivers

  • True prevalence (20,000-40,000) reconciled against the 3,000-4,000 currently treated
  • The 2,000-5,000/yr new-diagnosis rate since 2021 and why 15,000-36,000 patients remain undiagnosed regardless
02
What share of the UK ATTRv hereditary population is captured in the national registry, and what does that miss?

Delivers

  • 1,000-2,000 estimated ATTRv patients vs ~800 registered
  • Val30Met and Thr60Ala family clusters; NHS GMS gene panel access
03
What does the live, re-runnable funnel model contain, and how is every conversion step sourced?

Delivers

  • 8-sheet structure (Strategic Context, Inputs, Model, Projections, Sensitivity, References, Market Context, QC)
  • Live formulas, zero hardcoded cells; source citation per conversion step across ATTRwt-CM and ATTRv

Custom model delivered in 72 hours.

Commission This Model
Contents

What's inside

Rare Disease · 24–32 pp · In-Market · Analyst report + Excel model + PowerPoint readout

1 The Binding Constraint 2 pp
  • Why the Tc-PYP referral pathway, not NICE cost-effectiveness, sets the growth rate
  • Pressure-tested against the 2021 pre/post-Tc-PYP diagnosis-rate step change before the rest of the model is built out
2 Disease Burden (E1) — True Prevalence 3 pp
  • 20,000-40,000 true UK ATTRwt-CM prevalence estimate
  • 1,000-2,000 estimated ATTRv (hereditary) patients
3 Diagnosis & Capture (E2) — NHS Tc-PYP Pathway 4 pp
  • 2,000-5,000 new diagnoses per year since 2021, across 30 active NHS scintigraphy centres
  • The pre-2021 baseline of under 500 diagnoses per year
4 Subtype Eligibility (E3) — ATTRwt vs ATTRv Share 3 pp
  • Val30Met and Thr60Ala family clusters within the ATTRv population
  • ~800 patients tracked in the UK National ATTRv Registry against an estimated 1,000-2,000 total
5 Market Access (E4) — NICE-Commissioned Treatment Eligibility 3 pp
  • NICE TA984 (tafamidis) and TA1121/TA1115 (acoramidis, vutrisiran) commissioning routes
  • England's 90-day funding obligation vs devolved-nation divergence
6 Sensitivity Analysis 3 pp
  • Which assumptions move the undiagnosed-to-diagnosed conversion most
  • Scenario ranges for Tc-PYP referral-pathway expansion
7 Year 1·3·5 Projections 4 pp
  • Patient volume by horizon under conservative, base, and aggressive scenarios
  • Revenue translation inputs by sub-population
8 Client Alignment Questions 2 pp
  • The open questions your forecasting team must close before the model is finalised
  • Structured for an internal forecast-review session
Appendix and source ledger included · 45-minute analyst readout included with delivery
Formats

Included with every brief

PDF
PDF Brief
Patient Flow Brief — Complete Edition
PDF methodology brief accompanying the 8-sheet funnel model: true prevalence, NHS Tc-PYP diagnosis capture, subtype eligibility, and NICE-commissioned market access for UK ATTR amyloidosis across ATTRwt-CM and ATTRv.
XLS
Excel Model
Patient Flow Model — Excel
8-sheet editable funnel model: Strategic Context, Inputs, Model, Projections, Sensitivity, References, Market Context, QC. Live formulas, zero hardcoded cells.
PPT
PowerPoint
Executive Readout — PowerPoint
12-15 slide readout deck for forecasting and launch team presentations, formatted to AXLRx design standards.
Methodology

How AXLRx builds this model

Prepared by MoatRx analysts.

Every AXLRx patient flow model is built on a five-layer funnel: population, disease burden (E1), diagnosis and specialist capture (E2), treatment and biomarker eligibility (E3), market access (E4), then Year 1-3-5 projections across three scenarios. Delivered as a live Excel workbook, not a static table, across 8 sheets with zero hardcoded cells.

UK ATTR amyloidosis sources: AXLRx's own disease-landscape, competitive-intelligence, payer-HTA, and launch-readiness research base for the UK market, reconciling NHS Tc-PYP pathway diagnosis rates against true prevalence.

  • True UK ATTRwt-CM prevalence and undiagnosed pool verified against the AXLRx UK launch-readiness research base
  • NHS-commissioned tafamidis treated population and annual growth verified against the AXLRx UK launch-readiness research base and NICE TA984
  • Annual new-diagnosis rate since the 2021 Tc-PYP pathway verified against the AXLRx UK disease-landscape research base
  • ATTRv registry-tracked population verified against the AXLRx UK disease-landscape research base and the UK National ATTRv Registry
FAQ

Frequently asked questions

Deliverables
What formats are included with every model?
Every commissioned Patient Flow Model includes an editable 8-sheet Excel funnel model (Strategic Context, Inputs, Model, Projections, Sensitivity, References, Market Context, QC), a PDF methodology brief, and an optional executive readout deck for forecasting and launch team presentations. A 45-minute analyst readout call is included.
Sources
How is the epidemiology evidence verified?
AXLRx builds from its own verified disease-landscape, competitive-intelligence, payer-HTA, and launch-readiness research base, not secondary market-research summaries. Every conversion rate is cited to a source record and re-runnable in the model, not a black-box number.
Customisation
Can I tailor the cohort definition or comparator set?
Yes. The intake form captures your indication, target market, cohort definition, and comparators. A scoping call confirms scope before research starts. Commission via the intake form to start.
Get Started

Commission this model

AXLRx delivers rare-disease patient flow models built for forecasting and launch teams sizing the UK ATTR amyloidosis opportunity across ATTRwt-CM and ATTRv. Custom model in 72 hours.

1
Submit your request

Specify your indication, market, and cohort definition.

2
Scoping call

AXLRx analyst confirms funnel scope and comparator set before building.

3
Delivery

Research-verified patient flow model in 72 hours with optional analyst readout.